University team succeeds with gene therapy for hemophilia in mice

A group from Akitsu HOTTA Kyoto University and around Hideto MATSUI from Nara Medical University succeeded to cure hemophilic mice after transferring factor VIII usisng a non-viral piggyback vector as a vector. The mice when temporally treated with an immunosuppressant produced circulating factor VIII for over 300 days,

China Bio news release, August 18, 2014

Most popular posts: