Kyoto University and JST report dystrophin gene repair in iPS cells derived from a patient with Duchenne muscular dystrophy

Using genome editing technology based on TALEN and the CRISPR/Cas9 system, a group around Akutsu HOTTA succeeded to repair the dystrophin gene („exon 45 skipping“) in iPS cells derived from a DMD patient.

JST news release, Nov. 27, 2014

Kyoto University and JST report dystrophin gene repair in iPS cells derived from a patient with Duchenne muscular dystrophy
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