A group from Akitsu HOTTA Kyoto University and around Hideto MATSUI from Nara Medical University succeeded to cure hemophilic mice after transferring factor VIII usisng a non-viral piggyback vector as a vector. The mice when temporally treated with an immunosuppressant produced circulating factor VIII for over 300 days,
China Bio news release, August 18, 2014
University team succeeds with gene therapy for hemophilia in mice